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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Multi exon skipping
Cells
Delivery
Duchenne DMD dystrophy
Inbred C57BL
Energy Metabolism/drug effects
Long QT
Dystrophie Musculaire de Becker BMD
Epigenetics
Muscle Biology
MiARN
Long noncoding RNA
Gene modifiers
Mice
Cardiomyopathy
CD38
Gene Expression Regulation/drug effects
Diseases
Calcium
Metabolism
Duchenne muscular dystrophy DMD
Genomic
Multi resolution modeling
MES
Duchenne muscular dystrophy
DMO
Cardiomyopathie
Autophagy
Immunoglobulin Fc Fragments/pharmacology
Muscle
Human Umbilical Vein Endothelial Cells
Antisense oligonucleotides
Hepatocellular carcinoma
Clinical trials
L-Type
NNOS
LncRNA
CaVβs
Cell Line
Becker muscular dystrophy
Dystrophie Musculaire de Duchenne DMD
Centronuclear myopathy
Modificateurs de gènes
Becker BMD muscular dystrophy
Gene expression
Calcium Channels
Exon skipping
Male
Muscular Atrophy
Dystrophine
Mitochondrial fission
Muscular Dystrophy
Cell homeostasis
Muscle development
Becker muscular dystrophy BMD
Dystrophy
Génomique
Cachexia
Hear
Inhibitors
Myotendinous junction
Cultured
DMD
Cell Biology
Invivo
Animals
Dystrophie musculaire de Becker
DHPR α1S
Dystrophin
Multiresolution modeling
LncARN
BMD
Dystrophin-EGFP
Humans
Animal/physiopathology
Homeostasis
Myogenesis
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Ex-vivo
LKB1
Molecular docking
CTNNB1
CaV subunits
Skeletal muscle
Molecular Sequence Data
NAD+
Dynamin 2
Activin Receptors
Base Sequence
Dystrophin central domain
Morphogenesis
Knockout
Drp1
Allele‐specific silencing therapy
Muscular dystrophy
Liver
Muscles/physiopathology
Muscle Strength
Mdx mouse
Inbred mdx